Biomedical Pioneering Innovation Center
Contact

E-mail: jejrasko@gmail.com

Lab Web:

John Edward Joshua Rasko, AO
Guest Chair Professor

Resume

2026: Guest Chair Professor of BIOPIC, Peking University

2026: Visiting Professor, Macau University of Science and Technology

2025: Fellowships: Academia Europaea; Hungarian Academy of Sciences; Australian Academy of Technological Sciences and Engineering

2024: Honorary Doctor of Science, UTAR University

2015: Fellowship: Australian Academy of Health & Medical Sciences

1995: PhD, University of Melbourne, Walter and Eliza Hall Institute

1993: Fellowships: Royal Australasian College of Physicians (RACP) & Royal College of Pathologists of Australasia (RCPA)

1986: Bachelor of Medicine and Bachelor of Surgery, University of Sydney


Professional Experience

2018-2020: President, International Society for Cell & Gene Therapy

2008–2026: Chair, Gene Technology Technical Advisory Committee, Office of the Gene Technology Regulator

1999-2024: Founding Director & Head, Department of Cell & Molecular Therapies, Royal Prince Alfred Hospital

Board, Advisory & Consulting Roles (Pfizer, CSL Behring, Rarecyte, Cynata, Kennerton Capital, Woke Pharmaceuticals)

Research Interests

Professor John Rasko AO is a globally recognised leader in gene and cell therapy, regenerative medicine, and molecular biotechnology. As a clinical haematologist, pathologist and scientist, he has shaped the medical translation of advanced therapeutics in Australia and internationally. From 1999 to 2024, he directed the Department of Cell & Molecular Therapies at Royal Prince Alfred Hospital and the Gene & Stem Cell Therapy Program at the University of Sydney, building world-class programs bridging discovery and real-world impact.


Career Impact

Clinical trials development strategies (Phase I–III)
Gene & cell therapy
Translational & regenerative medicine
GMP manufacturing & quality oversight
Scientific communication & stakeholder engagement
Licensing, IP, and public-private partnerships
Regulatory & ethics leadership (GTTAC, WHO INN Committee, Biosafety & Ethics)

Awards and Honors

2025 HE Science Foundation Research Fellow

Public Service Award, ISSCR (2025)

Distinguished Fellow Award, RCPA (2013)

Officer of the Order of Australia (AO), 2012

Eric Susman Prize, RACP (2011)

Selected Publication & Invited Talks

NEJM (2025): First and corresponding author on haemophilia B gene therapy trial with multi-year follow-up.

Cell (2025): An alternate receptor for adeno-associated viruses

Book (2021): Flesh Made New: The Unnatural history and broken promise of stem cells, Harper Collins

Nature Medicine (2020 & 2024): First-completed iPSC-derived MSC trial for GvHD and two-year follow-up safety study.

NEJM (2018): Ex vivo lentiviral gene therapy for transfusion-dependent beta thalassemia (Zynteglo®).

Boyer Lectures (2018), ABC Radio/TV: 'Life Re-engineered'.

Science Translational Medicine (2017): International ‘Call to Action’ on unproven stem cell therapies.

Cell (2013) cell-specific intron retention as a mechanism that controls translation

Nature Medicine (2006 & 2007) landmark clinical trials “leading the way to a cure for hemophilia” - nearly 4000 citations